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| Sponsor / Funder | CINRG |
| CI | Professor Kate Bushby |
| Sites | Newcastle |
| Contact details | becky.davis@ncl.ac.uk |
| More information |
This is a multi-centre natural history study. It will be
conducted at Cooperative International Neuromuscular Research Group (CINRG)
sites and affiliated centres.
After a baseline evaluation, participants will
have three follow-up visits over three years.
We will characterize the BMD phenotype and link specific abnormal dystrophin proteins with the range of clinical outcomes.